Critical supply chain to save lives of very ill children designed and run from Ireland

Ireland is at the centre of a critical supply chain to treat children with a devastating and often fatal inherited condition. There are about 350 recorded cases of the condition though researchers suspect that is in part due to lack of familiarity with the condition and the difficulty in diagnosing it.

The PTC drug, called Upstaza, is the only known treatment. But to do its job, it has to be infused into the brain of the patient who might be as young as 18 months old. And, until then, it has to be kept in extremely cold conditions – below a temperature of -65 degrees.

In this article, Almac is described as the natural partner of choice for PTC when they required a supply chain design for this new drug.